Pipeline

Internal

Disorder / Target
Partner
Candidate ID
Preclinical
Clinical
Pain – Nav1.7 (ASO)
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Q-State - Owned
Pain – Nav1.8 (ASO)
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Q-State - Owned
Pain – Dual Nav1.7/1.8 (ASO)
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Q-State - Owned
Pain – Nav1.7 (Small Molecule)
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Q-State - Owned
Epilepsy - Dup15q Syndrome (ASO)
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Q-State - Owned
Monogenic Epilepsy (ASO)
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Q-State - Owned
Monogenic Epilepsy (ASO)
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Q-State - Owned

Partnered

Disorder / Target
Partner
Candidate ID
Preclinical
Clinical
Spastic Paraplegia Type 49
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TECPR2 Foundation
ALS Target
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QurAlis
Select Genetic Epilepsy
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UCB
Undisclosed Genetic Disorder
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Vertex