Pipeline
Internal
Disorder / Target
Partner
Candidate ID
Preclinical
Clinical
Pain – Nav1.7 (ASO)
Q-State - Owned
Pain – Nav1.8 (ASO)
Q-State - Owned
Pain – Dual Nav1.7/1.8 (ASO)
Q-State - Owned
Pain – Nav1.7 (Small Molecule)
Q-State - Owned
Epilepsy - Dup15q Syndrome (ASO)
Q-State - Owned
Monogenic Epilepsy (ASO)
Q-State - Owned
Monogenic Epilepsy (ASO)
Q-State - Owned
Partnered
Disorder / Target
Partner
Candidate ID
Preclinical
Clinical
Spastic Paraplegia Type 49
TECPR2 Foundation
ALS Target
QurAlis
Select Genetic Epilepsy
UCB
Undisclosed Genetic Disorder
Vertex